DMD: Charting the Path for New Therapeutics and Better Care - Webinar Agenda Trailer

Dear colleagues and friends, WuXi AppTec is proud to host the global event titled "Duchenne Muscular Dystrophy: Charting the Path for New Therapeutics and Better Care," which will take place on Sept. 9. The full agenda of this special event is now available. This complimentary event is co-organized with Parent Project Muscular Dystrophy (PPMD) and CureDuchenne. Over 20 top speakers, including drug developers, researchers, clinicians, and patients will share their insights in collaborating to find new therapeutics and better care. For the convenience of our global audience, the program will be aired on Zoom at 8am - 10:30am PDT (11am -1:30pm EDT) and 7pm - 9:30pm PDT (10pm - 12:30am EDT), respectively. We will send a replay link after the event to those who registered but couldn't make it or stay through the entire webinar. Please register for the event at this link: https://bit.ly/3sGbhIA AGENDA (Thursday, Sept. 9) for the 1st broadcast 8:00 am (PDT)/11:00 am (EDT) Welcome Hui Cai, VP and Head of Content, WuXi AppTec Pat Furlong, Founding President & CEO, Parent Project Muscular Dystrophy Debra Miller, CEO & Founder, CureDuchenne Filippo Buccella, Founder, Parent Project Italy APS Huigu Chen, President, Shanghai Jiai Myopathy Care Center, China Tali Kaplan, Co-Founder & CEO, Little Steps Association for Patients with Duchenne & Becker Muscular Dystrophy, Israel Sherena Loh, Director, Muscular Dystrophy Association (Singapore) 8:15 am (PDT)/11:15 am (EDT) Clinical Research and Practices Kevin Flanigan, Director, Center for Gene Therapy, Professor, Pediatrics & Neurology, Nationwide Children’s Hospital Stanley Nelson, Professor of Human Genetics, Center for Duchenne Muscular Dystrophy, David Geffen School of Medicine at UCLA Richard Parad, Associate Professor of Pediatrics, Harvard Medical School, Department of Pediatric Newborn Medicine, Brigham and Women’s Hospital Moderator: Hawken Miller, Features Writer, BioNews 8:45 am (PDT)/11:45 am (EDT) A Conversation between Pat Furlong, Founding President & CEO, Parent Project Muscular Dystrophy and Debra Miller, CEO & Founder, CureDuchenne 8:55 am (PDT)/11:55 pm (EDT) Patient Story - The Nilson Family 9:00 am (PDT)/12:00 am (EDT) What can we do to bring medicines to DMD patients around the world faster? Michael Binks, VP & Head of Clinical Research in the Rare Disease Research Unit at Pfizer Paula Clemens, Professor & Vice Chair, Neurology, University of Pittsburgh School of Medicine Nathalie Goemans, Professor, Neuromuscular Reference Centre for Children, Department of Pediatric Neurology, University Hospitals Leuven, Belgium Moderator: Timothy Franson, Principal, Faegre Drinker Consulting and formerly VP Global Regulatory Affairs, Eli Lilly & Co and Chief Medical Officer of YourEncore 9:30 am (PDT)/12:30 pm (EDT) New Targets. New Modalities. New Directions. Rhonda Bassel-Duby, Professor, Department of Molecular Biology, University of Texas Southwestern Medical Center Ashish Dugar, SVP & Global Head of Medical Affairs, Dyne Therapeutics Jane Larkindale, VP, Clinical Sciences, PepGen Art Levin, CSO, Avidity Biosciences Stuart Peltz, Founder & CEO, PTC Therapeutics Moderator: Richard Soll, Head of Boston Office and Senior Advisor of Strategic Initiatives, WuXi AppTec 10:20 am (PDT)/13:20 pm (EDT) 10-Year Vision Michael Binks, VP & Head of Clinical Research in the Rare Disease Research Unit at Pfizer Yi Dai, Associate Professor, Department of Neurology, Peking Union Medical College Hospital, China Xihua Li, Director, Department of Neuromuscular Disease, Children’s Hospital of Fudan University, China Stanley Nelson, Professor of Human Genetics, Center for Duchenne Muscular Dystrophy, David Geffen School of Medicine at UCLA Richard Parad, Associate Professor of Pediatrics, Harvard Medical School, Department of Pediatric Newborn Medicine, Brigham and Women’s Hospital Stacey Tay, Senior Consultant, Department of Paediatrics, Khoo Teck Puat - National University Children's Medical Institute, National University Hospital, Singapore 10:30 am (PDT)/13:30 pm (EDT) Closing Hui Cai, VP and Head of Content, WuXi AppTec